List of FDA Orphan Drugs | Genetic and Rare Diseases …

GARD has information from the Food and Drug Administration (FDA) on treatments approved for rare diseases, known as orphan products/drugs. The Orphan Drug Act was passed in 1983 to give drug companies incentives to develop treatments for rare diseases. The FDA Office of Orphan Products Development determines if a drug qualifies as an orphan product.

https://rarediseases.info.nih.gov/diseases/fda-orphan-drugs