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 Posted in Web

Spinraza is Approved! | Muscular Dystrophy Association

 July 18, 2019

Spinraza is a disease-modifying antisense drug, one of a class of experimental therapeutic molecules designed to target genetic instructions at the RNA stage (an intermediate step between DNA and protein manufacturing stage inside cells). It is designed to increase production of the needed SMN protein.

: https://www.mda.org/spinraza

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